Sickle cell disease (SCD) is a group of inherited blood disorders resulting from a mutation in the hemoglobin protein in red blood cells. This mutation changes the shape of the blood cells from round, ...
Anemia poses a significant public health challenge, primarily impacting the health of young children, pregnant and postpartum women, as well as menstruating adolescent girls and adult women. On a ...
Sickle cell disease (SCD) is an inherited disorder that affects over 100,000 people in the United States, according to the Sickle Cell Disease Association of America, of that number, the Centers for ...
Sickle cell anemia is the world's most common genetic disorder. It causes the red blood pigment hemoglobin to crystallize, ...
Exagamglogene autotemcel (exa-cel), a CRISPR/Cas9 gene-edited cell therapy, eliminated vaso-occlusive crises in 97% of participants with severe sickle cell disease. The therapy led to substantial ...
CS-101 is Shanghai-based CorrectSequence's lead candidate, which it is developing for treating sickle-cell disease and ...
Sickle cell disease (SCD) is a group of genetic blood disorders. A person inherits SCD from their parents when they inherit two copies of the sickle cell gene, one from each parent. This hereditary ...